Support Our Cause: Donate

We are currently collaborating with various organisations to raise essential funds to support galactosialidosis treatment initiatives.

Our primary focus is on securing funding for the forthcoming gene therapy program conducted by UMass Chan Medical Hospital in conjunction with Great Ormond Street Hospital (UK), pending FDA approval. We anticipate receiving the FDA decision by 24 February 2024.

We would like to have the necessary funds readily available to support access to clinical trials and treatment opportunities as they progress. Time is of the essence as each passing day poses further challenges for affected individuals and we need to act fast.

We sincerely appreciate your contribution and encourage you to use the ISMRD website for donations, specifying “galactosialidosis” in the reference section when making a payment.


Get in touch

If you would like more info or would like to collaborate with us to help find a treatment, please contact us using the details below:

You can also join the ISMRD mailing list.

International Directory of Clinicians and Scientists with experience of galactosialidosis are cited here, if you are a patient, parent or professional with an interest in galactosialidosis you may want to get in touch.